印度科学家利用慢病毒载体技术完成了印度首次针对A型血友病基因治疗的人体临床试验。 Indian scientists completed India's first human clinical trial of gene therapy for Haemophilia A using lentiviral vector technology.
CMC Vellore 的印度科学家完成了该国首次针对 A 型血友病基因治疗的人体临床试验,这是一种影响印度约 136,000 人的遗传性疾病。 Indian scientists at CMC Vellore completed the country's first human clinical trial of gene therapy for Haemophilia A, a genetic disorder affecting around 136,000 people in India. 该试验使用新型慢病毒载体技术在患者的造血干细胞中表达 FVIII 转基因。 The trial used a novel lentiviral vector technology to express FVIII transgene in patients' haematopoietic stem cells. 科技部长宣布载体生产即将在印度开始,为进一步的临床试验铺平道路。 The Minister of Science & Technology announced that the vector manufacturing will soon commence in India, paving the way for further clinical trials.