洛杉矶新生儿在接受突破性基因编辑疗法后,从罕见的遗传疾病中恢复过来,这标志着个性化医学的一个里程碑。
A Los Angeles newborn recovered from a rare genetic disorder after receiving groundbreaking gene-editing therapy, marking a milestone in personalized medicine.
洛杉矶的新生儿在接受了针对一种罕见的、威胁生命的基因障碍的先导基因编辑治疗后,已经出院,这标志着个性化医学的重大进步。
A newborn in Los Angeles has been discharged after receiving a pioneering gene-editing therapy for a rare, life-threatening genetic disorder, marking a major advance in personalized medicine.
这一治疗纠正了特定的基因突变,使婴儿得以康复并返回家园。
The treatment, which corrected a specific genetic mutation, enabled the infant’s recovery and return home.
包括Kiran Musunuru博士在内的研究人员说,这一成功为治疗其他极端罕见的遗传条件带来了希望,尽管治疗仍处于早期阶段,需要进一步发展,才能更广泛地使用。
Researchers, including Dr. Kiran Musunuru, say the success offers hope for treating other ultra-rare genetic conditions, though the therapy remains in early stages and requires further development before broader use.