9岁的Andy Cash通过基因治疗治愈了罕见的免疫障碍,使正常生活和接种疫苗成为可能。 Nine-year-old Andy Cash cured of rare immune disorder via gene therapy, enabling normal life and vaccinations.

来自Portlaoise的九岁的Andy Cash(来自Portlaoise的Andy Cash)在三周前被诊断为ADA-SCID, 在伦敦Great Ormond街医院的一次基因治疗试验中取得了改变生命的成果。 Nine-year-old Andy Cash from Portlaoise, diagnosed with ADA-SCID at three weeks old, has achieved life-changing results from a gene therapy trial at London’s Great Ormond Street Hospital. 稀有的免疫紊乱使他容易受致命感染,通过开创性疗法治疗,利用自己的细胞纠正他的遗传缺陷。 The rare immune disorder, which left him vulnerable to fatal infections, was treated through a groundbreaking therapy that corrected his genetic defect using his own cells. 在联合王国-美国试验的62名病人中,95%实现了长期治疗,使正常的免疫功能和常规疫苗接种成为可能。 Of 62 patients in the UK-US trial, 95% achieved long-term cure, enabling normal immune function and routine vaccinations. Andy,现在能够自由生活,社交, 和盒子, 代表着治疗遗传疾病的重大进步。 Andy, now able to live freely, socialize, and box, represents a major advance in treating genetic diseases.