中国科学家研发基因疗法注射, 可以恢复视网膜炎色素患者的视力。 Chinese scientists develop gene therapy injection that could restore vision for retinitis pigmentosa patients.

中国研究人员开发了基因疗法注射,部分恢复了视网膜炎色素(RP)患者的视力,这一病情影响到4 000人中的1人。 Chinese researchers have developed a gene therapy injection that partially restores vision for patients with retinitis pigmentosa (RP), a condition affecting about 1 in 4,000 people. 由Loo Minmin教授牵头,该团队使用重新组合的肾上腺相关病毒向眼睛提供一种基因编码,即轻度敏感的鸡蛋白质,只需简单注射即可。 Led by Professor Luo Minmin, the team used a recombinant adeno-associated virus to deliver a gene encoding a light-sensitive chicken protein into the eye, requiring only a simple injection. GA001治疗可以到2025年底进入临床试验阶段,为病人恢复一些视力而不进行侵入性外科手术提供了希望。 The treatment, GA001, could progress to clinical trials by the end of 2025 and offers hope for patients to regain some vision without invasive surgery.