婴儿KJ Muldoon因罕见疾病而接受CRISPR治疗,因健康状况改善而出院。
Baby KJ Muldoon, treated with CRISPR for a rare disease, discharged from hospital with improved health.
KJ Muldoon是最早在费城儿童医院接受CRISPR基因编辑治疗的最年轻的病人,10个月的KJ Muldoon在其罕见代谢疾病CPS1成功治疗后出院。
Ten-month-old KJ Muldoon, the youngest patient to receive CRISPR gene-editing therapy at Children's Hospital of Philadelphia, was discharged after successful treatment for his rare metabolic disease, CPS1.
尽管治疗尚未治愈他,但治疗大大改善了他的病情。
The therapy has significantly improved his condition, though it has not cured him.
KJ的返校节庆祝活动得到了警方的护送和社区的支持,这是CRISPR治疗罕见疾病技术的一个重要里程碑。
KJ's homecoming was celebrated with a police escort and community support, marking a major milestone in CRISPR technology for treating rare diseases.