基因治疗突破使得患有严重免疫疾病的男孩能够过正常生活。
Gene therapy breakthrough allows boy with severe immune disease to lead a normal life.
Eisa Hussain是患有严重免疫疾病血清粘合症1(LAD-1)的男孩,通过突破性基因疗法,得以过上正常生活。
A groundbreaking gene therapy has enabled Eisa Hussain, a boy with the severe immune disease leukocyte adhesion deficiency 1 (LAD-1), to lead a normal life.
以前,LAD-1的病人通常在2岁前死亡,没有干细胞移植,需要近距离捐献。
Previously, patients with LAD-1 typically died before age two without a stem cell transplant, which required a close-match donor.
新疗法对病人的细胞进行改造,以生产防治感染的关键蛋白质。
The new therapy modifies the patient's cells to produce a crucial protein for fighting infections.
Eisa在Great Ormond街医院接受治疗后, 现在可以走路、上学、享受足球等活动,
After receiving the treatment at Great Ormond Street Hospital, Eisa can now walk, attend school, and enjoy activities like football.