年轻的纽约人治愈了镰状细胞贫血 通过破土基因疗法, 利夫盖尼亚。
Young New Yorker cured of sickle cell anemia with groundbreaking gene therapy, Lyfgenia.
Sebastien Beauzile, 21岁来自纽约, 成为该州第一位使用新基因疗法(Lyfgenia)治愈镰状细胞贫血的病人。
Sebastien Beauzile, a 21-year-old from New York, has become the first patient in the state to be cured of sickle cell anemia using a new gene therapy called Lyfgenia.
这种治疗改变病人的骨髓以产生健康的红细胞,给有这种症状的其他人带来希望,这主要影响到非洲、地中海和中东血统的人。
The treatment modifies the patient's bone marrow to produce healthy red blood cells, offering hope to others with the condition, which primarily affects people of African, Mediterranean, and Middle Eastern descent.
公民权利律师Ben Crump捐助了100 000美元,以支持进一步的治疗工作。
Civil rights attorney Ben Crump donated $100,000 to support further treatment efforts.