伦敦医生通过新的基因疗法改善4名失明罕见儿童的视力。 London doctors improve vision in four children with rare blindness through new gene therapy.

伦敦的医生利用先锋基因疗法,成功地治疗了4名失明的幼儿,他们患有罕见的失明形式,叫做Leber Congenital Amaurosis(LCA)。 Doctors in London have successfully treated four young children with a rare form of blindness called Leber Congenital Amaurosis (LCA) using a pioneering gene therapy. 治疗包括将ALPL1基因的健康拷贝注入视网膜,这大大改善了儿童的视力,使他们能够看到形状,甚至读写。 The treatment involves injecting healthy copies of the AIPL1 gene into the retina, which significantly improved the children's vision, enabling them to see shapes and even read and write. 这种开创性疗法为其他遗传失明儿童提供了希望。 This groundbreaking therapy offers hope for other children with genetic blindness.